earnings
confidence high
sentiment positive
materiality 0.75
Ultragenyx Q2 revenue $147M (+36% YoY), raises 2024 guidance; key FDA agreements advance pipeline
Ultragenyx Pharmaceutical Inc.
2024-Q2 EPS reported
-$3.54
revenue$255,859,000
- Q2 total revenue $147M (Crysvita $114M, Dojolvi $19M); net loss narrows to $132M from $160M.
- 2024 revenue guidance raised to $530-550M (prev $500-530M); Crysvita expected towards upper end of $375-400M.
- Cash $874M after June equity offering of $381M net; 2024 operating cash use guided below $400M.
- FDA agrees CSF heparan sulfate as surrogate endpoint for UX111 Sanfilippo accelerated approval; BLA filing late-2024/early-2025.
- Positive Phase 3 data for DTX401 in GSDIa (41.3% reduction in cornstarch, p<0.0001); Phase 2/3 OI setrusumab shows 67% fracture reduction.