earnings
confidence high
sentiment positive
materiality 0.80
Ultragenyx preliminary 2024 revenue $555-560M above guidance; 2025 guide $640-670M
Ultragenyx Pharmaceutical Inc.
2024-FY EPS reported
-$6.29
revenue$560,230,000
- Preliminary 2024 total revenue $555-560M, exceeding top end of guidance, ~29% YoY growth.
- Crysvita revenue $405-410M (+24% YoY); Dojolvi revenue $87-89M (+25% YoY).
- 2025 total revenue guidance $640-670M; cash and investments ~$745M as of Dec 31, 2024.
- UX143 Phase 3 OI study second interim analysis mid-2025; GTX-102 Phase 3 Angelman enrollment completion H2 2025.
- UX111 BLA submitted (PDUFA H2 2025); DTX401 BLA filing mid-2025; DTX301 Phase 3 enrollment early 2025.