earnings
confidence high
sentiment neutral
materiality 0.65
PTC Therapeutics Q2 revenue $187M; net loss narrows to $99M; NDAs submitted
PTC THERAPEUTICS, INC.
2024-Q2 EPS reported
-$2.49
revenue$396,822,000
- Q2 total revenue $186.7M vs $213.8M YoY; DMD franchise $118M (Translarna $70M, Emflaza $47M).
- Net loss $99.2M improved from $198.9M loss; cash $1.09B after $250M Royalty Pharma put option.
- Submitted NDA for sepiapterin (PKU) and resubmitted NDA for Translarna (nmDMD) to FDA in July 2024.
- Full-year 2024 revenue guidance $700M-$750M; GAAP R&D+SG&A $740M-$835M.
- BLA for AADC deficiency gene therapy accepted with priority review; PDUFA date Nov 13, 2024.