regulatory
confidence high
sentiment positive
materiality 0.60
FDA grants orphan drug designation to aTyr Pharma's efzofitimod for systemic sclerosis
aTYR PHARMA INC
- FDA granted orphan drug designation for efzofitimod to treat systemic sclerosis (scleroderma) on April 12, 2022.
- Orphan designation may provide 7-year market exclusivity, tax credits, and waiver of FDA fees.
- Efzofitimod is aTyr's lead therapeutic candidate; this designation supports its development program.