regulatory
confidence high
sentiment positive
materiality 0.90
FDA approves X4 Pharma's XOLREMDI for WHIM syndrome; pricing set at $496,400/yr
X4 Pharmaceuticals, Inc
- XOLREMDI (mavorixafor) approved for WHIM syndrome patients aged 12+ to increase neutrophils and lymphocytes.
- Wholesale acquisition cost: $496,400/yr (patients >50 kg, 400 mg daily) and $372,300/yr (≤50 kg, 300 mg daily).
- Launch through specialty pharmacy PANTHERx Rare; X4Connect support program offers copay assistance and insurance help.
- Corporate presentation posted on company website providing business updates.