PTC THERAPEUTICS, INC. (PTCT): restructuring charge — PTC discontinues early gene therapy programs, CFO terminated, vatiquinone Phase 3 misses primary endpoint
PTC THERAPEUTICS, INC.
- Discontinues preclinical/early gene therapy programs; workforce reduction of ~8%; expects 15% OPEX savings in 2023; severance costs ~$7M.
- CFO Emily Hill terminated effective immediately; employment ends Aug 20, 2023; eligible for severance without cause.
- Phase 3 MOVE-FA trial of vatiquinone in Friedreich ataxia misses primary endpoint (mFARS change, p=0.14). Subscales and completers analysis show signals.
- Company to discuss potential registration path with regulators despite missing primary endpoint; vatiquinone well tolerated.